
FDA-Approved Gene Therapy Reverses Blindness in Children & Adults
Published on Apr 23
13分钟
0:000:00
Host: Jennifer Caudle, DO <br>
Guest: Jean Bennett, MD, PhD <br>
Guest: Albert Maguire, MD <br>
<p><span class="mceitemhidden"><span>Power couple </span><span class="mceitemhiddenspellword"><span>Drs</span></span></span><span class="mceitemhidden"><span>. Jean Bennett and Albert Maguire discuss how their new therapy for the RPE65 gene, which causes retinal blindness, was recently approved by the FDA to become the first gene therapy treatment for a genetic disease in the United States <i>and</i> the first worldwide treatment for inherited blindness. Not only do they delve into the mechanics of the corrected gene injection, but they also explain what this milestone means for patient eligibility and how their marriage has played a role in the success of their research partnership.</span></span></p> <p><span class="mceitemhidden"><span>Dr. Jean Bennett is the F.M. Kirby Professor of Ophthalmology at the Perelman School of Medicine at the University of Pennsylvania, and D...